Prospective exploratory muscle biopsy, imaging, and functional assessment in patients with late-onset Pompe disease treated with alglucosidase alfa: The EMBASSY Study

Ans van der Ploeg, Pierre G. Carlier, Robert Yves Carlier, John T. Kissel, Benedikt Schoser, Stephan Wenninger, Alan Pestronk, Richard J. Barohn, Mazen M. Dimachkie, Ozlem Goker-Alpan, Tahseen Mozaffar, Loren D.M. Pena, Zachary Simmons, Volker Straub, Michela Guglieri, Peter Young, Matthias Boentert, Pierre Yves Baudin, Stephan Wens, Raheel ShafiCarl Bjartmar, Beth L. Thurberg

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